Ex Vivo Expansion of Hematopoietic Stem and Progenitor Cells from Human Mobilized Peripheral Blood for Gene Therapy Applications
Erika Zonari, Matteo Maria Naldini, Matteo Barcella, Monica Volpin, Francesca Vincenti, Giacomo Desantis, Leila Hadadi, Carolina Caserta, Ilaria Galasso, Beatrice Martini, Federico Midena, Giacomo Farina, Roberta Vacca, Francesca Tucci, Leonardo Ormoli, , Bernhard Gentner
This study optimizes an ex vivo expansion protocol for mobilized peripheral blood HSCs, enabling robust gene therapy applications with long-term engraftment.
Molecular Therapy · May 26, 2026Peer-reviewedCell Biology