NeuroscienceJournal of Huntington s DiseasePeer-reviewed
iPSC Neurodegenerative Disease Initiative isogenic CAG repeat iPSC line for Huntingtons disease
Lisa Salazar, Mara S. Burns, Jennifer T. Stocksdale…·Leslie Michels Thompson
The paper generates isogenic iPSC lines with CAG repeats and HTT KO for Huntington's disease study, showing differentiation potential and altered gene expression in neurons and astrocytes.
DOI 10.1177/18796397261497434