TFU72 is a novel and potent DNA-PKcs inhibitor for enhancing homology-directed repair gene editing
Sridhar Selvaraj, Ludwig Schmiderer, Jacob Lamberth, Thomas Fuchß, Freja K. Ekman, Norman F. Russkamp, Matthew Hebden Porteus
The paper introduces TFU72, a potent DNA-PKcs inhibitor that significantly enhances HDR gene editing efficiency while mitigating genotoxic side effects.
bioRxiv · Mar 11, 2026 · PreprintMolecular Biology