A temperature-sensitive and interferon-silent Sendai virus vector for CRISPR-Cas9 delivery and gene editing in primary human cells
Christian S. Stevens, Jillian C. Carmichael, Ruth Watkinson, Shreyas Kowdle, Rebecca A. Reis, Kory Hamane, Jason Jang, Arnold Park, Olivier Pernet, Wannisa Khamaikawin, Patrick W.-P. Hong, Patricia A. Thibault, Aditya Gowlikar, Dong Sung An, Benhur Lee
This paper develops a temperature-sensitive and interferon-silent Sendai virus vector for CRISPR-Cas9 delivery, achieving high gene editing efficiency in human cells without triggering immune responses.
Journal of Virology · Nov 4, 2024Peer-reviewedMicrobiology