NeurosciencebioRxivPreprint
AAV delivery of GBA1 suppresses alpha-synuclein accumulation in Parkinson's disease models and restores motor dysfunction in a Gaucher's disease model
Takuro Okai, Sho Sato, Mugdha Deshpande…·Gabriele Proetzel
This paper shows that delivering GBA1 via AAV reduces alpha-synuclein aggregates and restores motor function in disease models.
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