Mini-Pcdh15b Gene Therapy Rescues Visual Deficits in a Zebrafish Model of Usher Syndrome Type 1F
Xinlan Chen, Daniel M. Hathaway, Alex J. Klein, Jennifer B. Phillips, Kevin T. A. Booth, Muriel Heitsch, Anton Lytvyn, Bruce H. Derfler, Jeremy Wegner, Corey Goldstein, Andrew Murphy, Sean G. Megason, Monte Westerfield, David P. Corey, Maryna V. Ivanchenko
This paper shows that a gene therapy using a shortened PCDH15 variant rescues vision in a zebrafish model of Usher Syndrome Type 1F.
bioRxiv · Nov 5, 2025 · PreprintNeuroscience