Preclinical Screening of Splice-Switching Antisense Oligonucleotides in PDAC Organoids
L. Wan, A. J. Kral, D. Voss, A. Krainer
This study develops an efficient ASO transfection method to screen splicing events in PDAC organoids for therapeutic targets.
bioRxiv · Mar 31, 2023 · PreprintPharmacology & Toxicology