Ketosis rescues frataxin deficiency and corrects disease phenotypes in an FRDA animal model
Yina Dong, Miniat W. Adeshina, Ryan Smith, Lucie Vanessa Ngaba, Jacob An, Olivia Seline, Jennifer Coulman, Shahd Al Haj Ali, Clementina Mesaros, Peining Jimmy Xu, David R. Lynch
This study shows that ketosis increases frataxin levels and improves disease symptoms in a Friedreich ataxia mouse model.
bioRxiv · Jan 14, 2026 · PreprintBiochemistry