Zebrafish models for human ALA-dehydratase-deficient porphyria (ADP) and hereditary coproporphyria (HCP) generated with TALEN and CRISPR-Cas9
Shuqing Zhang, Jiao Meng, Zhijie Niu, Yikai Huang, Jingjing Wang, Xiong Su, Yi Zhou, Han Wang
This paper generates zebrafish models for human ALA-dehydratase-deficient porphyria and hereditary coproporphyria using TALEN and CRISPR-Cas9, revealing phenotypes similar to human diseases.
bioRxiv · Feb 17, 2017 · PreprintGenetics