A light-responsive lipid nanoparticle platform delivering Cas9 RNP for VEGFA editing suppresses choroidal neovascularisation
Rui Sang, Xinpu Yang, Ewa Magdalena Goldys, Yagiz Alp Aksoy, Gerald Liew, Wei Deng
This study develops a light-responsive lipid nanoparticle platform for VEGFA gene editing to suppress choroidal neovascularisation, showing reduced vascular leakage and structural abnormalities in a rat model.
bioRxiv · Oct 27, 2026 · PreprintBioengineering