Novel Muscle-Tropic AAV Capsids with Dramatically Enhanced Transduction and Safety Profiles in Non-Human Primates
Youguang Luo, Linlin Zhang, Zhenhua Wang, Hao Li, Rui He, Xiaofei Lv, Xianggang Xu, Shengwen Wang, Zhen Sun, Mengmeng Yu, Qun Zhang, Peilu Zhao, Long Wang, Bo Sun, Daoyuan Li, Zhenming An
The paper engineers AAV capsids with improved muscle transduction and reduced off-target distribution in non-human primates using the REACH platform.
bioRxiv · May 26, 2026 · PreprintBioengineering