GeneticsNature CommunicationsPeer-reviewed
Functional Profiling of Single CRISPR/Cas9-Edited Human Long-Term Hematopoietic Stem Cells
Elvin Wagenblast, Maria Azkanaz, Sabrina A. Smith…·Eric R. Lechman
The paper develops a method to efficiently edit LT-HSCs at single-cell resolution and demonstrates distinct functional outcomes of GATA1 editing.
49 citations