Benchmarking organ-specific responses to therapies in tissues differentiated from Cystic Fibrosis patient derived iPSCs
A. Daoud, S. Xia, O. Laselva, J. X. Jiang, C. Bear
This study benchmarks Trikafta's efficacy in CF patient-derived iPSC-derived colonic and airway tissues compared to isogenic controls, showing differential therapeutic responses.
bioRxiv · Mar 13, 2024 · PreprintPharmacology & Toxicology