BioengineeringbioRxivPreprint
A TLS11a-decorated ionizable lipid nanoparticle platform and a multilevel-validated CRISPR LDLR-knockout HepG2 model for hepatocyte-preferential mRNA delivery
Irfan Hussain, Naji Kholaif, Raghad Alsultan…·Farhatullah Syed
The paper develops an LDLR-independent LNP platform for hepatocyte-targeted mRNA delivery and validates an LDLR-knockout HepG2 model for studying LDLR biology.
DOI 10.64898/2026.07.21.739738