BiochemistrybioRxivPreprint
Extracellular vesicles derived from cells overexpressing HGSNAT rescue defects in Mucopolysaccharidosis IIIC neurons
Travis Mooree, Mahsa Taherzadeh, Xuefang Pan…·Alexey V. Pshezhetsky
The paper shows that extracellular vesicles from HGSNAT-overexpressing cells can rescue MPS IIIC neuron defects by delivering the enzyme to lysosomes.
DOI 10.64898/2026.07.22.740105