Cell BiologybioRxivPreprint
Targeted DUX4 base editing improves muscle function in an iPSC-derived model of childhood-onset FSHD
Peter J. Houweling, Vanessa G. Crossman, Leonit Kiriaev…·Ian R. Woodcock
This study uses iPSC-derived muscle models to show that DUX4 base editing improves muscle function in childhood-onset FSHD.
DOI 10.64898/2026.07.28.741079