Animal Behavior & CognitionbioRxiv
Oral Glucosamine Ameliorates Aggravated Neurological Phenotype in Mucopolysaccharidosis III Type C Mouse Model Expressing Misfolded HGSNAT Variant
X. Pan, M. Taherzadeh, P. Bose…·A. V. Pshezhetsky
This study shows oral glucosamine improves neurological symptoms in a mouse model with misfolded HGSNAT due to a Pro304Leu mutation.
DOI 10.1084/jem.20211860