Cell BiologybioRxiv
Human cellular model systems of β-thalassemia enablein-depth analysis of disease phenotype
D. E. Daniels, I. Ferrer-Vicens, J. Hawksworth…·J. Frayne
This study creates human cellular models of β-thalassemia to analyze disease phenotype and develops an assay to assess treatment responses.
DOI 10.1038/s41467-023-41961-9