Genetic & Genomic MedicineOrphanet Journal of Rare DiseasesPeer-reviewed
Utilization of CoRDS Registry to Monitor Quality of Life in Patients with VCP Multisystem Proteinopathy
Eiman Abdoalsadig, Merwa Hamid, Allison Peck…·Virginia E. Kimonis
This study uses the CoRDS registry to track quality of life in VCP disease patients, finding significant declines in mobility and function over time.
2 citations