Molecular BiologyHuman Gene TherapyPeer-reviewed
Development of a recombinant adeno-associated virus vector for human T lymphocyte- and natural killer cell-targeted gene therapy
Hendrik Jahnz, Martin V. Hamann, H.O. Kim…·Ulrike C. Lange
This paper develops a CD7-targeted rAAV vector for efficient gene delivery to human T and NK cells, showing reduced off-target effects and improved transgene expression through genome optimization.
DOI 10.1177/10430342261487919