Cell BiologybioRxivPreprint
Engineered tRNA suppression of a CFTR nonsense mutation
John D. Lueck, Daniel T. Infield, Adam L. Mackey…·Christopher A. Ahern
This paper demonstrates the use of engineered tRNA to suppress a CFTR nonsense mutation, rescuing full-length protein function in a cystic fibrosis model.
DOI 10.1101/088690