BioengineeringbioRxivPreprint
Efficient in vivo genome editing mediated by stem cells-derived extracellular vesicles carrying designer nucleases
S. Bobis-Wozowicz, K. Kania, K. Nit…·E. Zuba-Surma
This study demonstrates that stem cell-derived extracellular vesicles can deliver designer nucleases in vivo, achieving up to 50% gene knockout in the liver.
DOI 10.1101/2021.02.25.432823