NeuroscienceEMBO Molecular MedicinePeer-reviewed
Modeling Genetic Epileptic Encephalopathies using Brain Organoids
Daniel J Steinberg, Srinivasarao Repudi, Afifa Saleem…·Rami I. Aqeilan
This study uses brain organoids to model WOREE, a severe epileptic encephalopathy, identifying CNS abnormalities and showing potential therapeutic rescue via WWOX expression.
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