BioengineeringbioRxiv
Quantitative single-cell transcriptome-based ranking of engineered AAVs in human retinal explants
Z. Xi, B. E. Ozturk, M. E. Johnson…·L. C. Byrne
This study ranks engineered AAVs in human retinal explants using single-cell RNA-Seq, identifying top-performing serotypes for retinal gene therapy.