NeurosciencebioRxivPreprint
Computational drug repurposing identifies N-acetylglucosamine as a potential therapeutic compound for CLN3 Batten disease
Elina Casoli, Amali S. Fernando, Juliana C.S. Chaves…·Lotta E. Oikari
The paper uses computational drug repurposing to identify N-acetylglucosamine as a potential therapy for CLN3 Batten disease, showing it reduces lipofuscin burden in cell models.
DOI 10.64898/2026.05.12.724723