BioengineeringJournal of Controlled ReleasePeer-reviewed
Intravenous lipid-siRNA conjugate mediates gene silencing at the blood-brain barrier and blood-CSF barrier
Alexander G. Sorets, Katrina R Schwensen, Nora Francini…·Ethan S. Lippmann
This paper demonstrates that an intravenous lipid-siRNA conjugate can deliver gene silencing to brain barriers without affecting parenchymal tissue.