Tacrolimus Rescues Endothelial ALK1 Loss-Of-Function Signaling And Improves HHT Vascular Pathology
S. Ruiz, P. Chandakkar, H. Zhao, J. Papoin, P. K. Chatterjee, E. Christen, C. N. Metz, L. Blanc, F. Campagne, P. Marambaud
This study identifies tacrolimus as a drug that activates Smad1/5/8 signaling and reduces vascular pathology in HHT models.
bioRxiv · May 13, 2017Cell Biology