NeuroscienceScientific ReportsPeer-reviewed
Duchenne Muscular Dystrophy Cell Culture Models Created By CRISPR/Cas9 Gene Editing And Their Application To Drug Screening
Patricia Soblechero‐Martín, E. Albiasu-Arteta, Aina Anton…·Virginia Arechavala‐Gomeza
The paper describes CRISPR/Cas9-generated Duchenne muscular dystrophy cell models for drug screening, showing successful exon deletion and utrophin upregulation.
20 citations