Cell BiologySkeletal MusclePeer-reviewed
Deletion of exons 45 to 55 in the DMD gene: from the therapeutic perspective to the in vitro model
Javier Poyatos‐García, Patricia Soblechero‐Martín, Alessandro Liquori…·Juan Jesus Vilchez
The paper restores dystrophin expression in DMD cells by replicating a specific exon deletion and creates a new cell model to study the mutation's effects.
4 citations