Cell BiologybioRxivPreprint
Ryanodine receptor 1 ( RYR1 ) patient-derived muscle cells recapitulate disease phenotypes in 2D and 3D culture models
Joshua S. Clayton, Jordan Crane, Jeremy D. D. Garcia…·Rhonda L. Taylor
This study uses patient-derived iPSCs to create 2D and 3D muscle models that replicate RYR1 myopathy phenotypes and test therapeutic efficacy.
DOI 10.64898/2026.06.18.732485