A Human Genetics Framework for De-risking Gene Editing Targets for Hematopoietic Cell and Gene Therapy
Abhinav Dhall, Alyssa Pyclik, Matthew H. Ung, Julia Etchin, Yonina Keschner, Huanying Gary Ge, Tirtha Chakraborty, John R. Lydeard
The paper develops a proteogenomic framework to identify dispensable genes for safer gene editing in hematopoietic therapies, identifying 237 candidates including LY75.
bioRxiv · Dec 17, 2025 · PreprintGenetics