NeurosciencebioRxivPreprint
Antisense oligonucleotide therapy for SCN2A gain-of-function epilepsy
Melody Li, Nikola Jancovski, Paymaan Jafar‐Nejad…·Steven Petrou
This study shows that reducing SCN2A function with an antisense oligonucleotide improves survival and behavior in a mouse model of early seizure onset DEE.
13 citations