Cell BiologybioRxivPreprint
Translational lipidomics reveals BMP and its precursor LPG as biomarkers for CLN5 Batten disease
Eshaan S. Rawat, Nick Manfred, Hisham N. Alsohybe…·Monther Abu-Remaileh
This study identifies BMP and LPG as biomarkers for CLN5 Batten disease using lipidomics, showing their depletion and elevation in disease models and patient samples.