Molecular BiologyMolecular Therapy — Methods & Clinical DevelopmentPeer-reviewed
Transcriptional changes in non-human primate tissues after intrathecal delivery of serotype 9 adeno-associated viral vector: insights into organ toxicities
Fumiaki Aihara, Mathew Mardo, Vera M. Ruda…·Eloïse Hudry
This study examines transcriptional changes in non-human primate tissues after AAV9 vector delivery, finding significant immune-related gene upregulation in liver and DRG.