NeuroscienceJournal of Controlled ReleasePeer-reviewed
Lipid nanoparticle-mediated CRISPR/Cas9 delivery enables efficient trabecular meshwork gene editing in mice
Yifan Huang, Silin Pang, Linxian Li…·Wenjun Xiong
This study demonstrates that lipid nanoparticle-mediated CRISPR/Cas9 delivery efficiently edits genes in the trabecular meshwork of mice, inducing glaucoma-like features.
6 citations