BiochemistrybioRxiv
Diverse lipid conjugates for functional extra-hepatic siRNA delivery in vivo
A. Biscans, A. Coles, R. Haraszti…·A. Khvorova
This study develops lipophilic conjugates to enable siRNA delivery to extra-hepatic tissues, showing effective gene silencing in multiple organs.
DOI 10.1093/nar/gky1239