Cell BiologybioRxiv
Prednisolone rescues Duchenne Muscular Dystrophy phenotypes in human pluripotent stem cells-derived skeletal muscle in vitro
Z. Al Tanoury, J. F. Zimmermann, J. Rao…·O. Pourquie
This study shows prednisolone rescues DMD phenotypes in iPSC-derived muscle cells, suggesting direct myofiber effects rather than just anti-inflammatory benefits.
DOI 10.1073/pnas.2022960118