Prime editing enables precise genome editing in mouse liver and retina
H. Jang, J. H. Shin, D. H. Jo, J. H. Seo, G. Yu, R. Gopalappa, S.-R. Cho, J. H. Kim, H. H. Kim
This study demonstrates that prime editing can correct disease-causing mutations in adult mouse liver and retina, with minimal off-target effects.
bioRxiv · Jan 8, 2021 · PreprintBioengineering