NeuroscienceCell ReportsPeer-reviewed
In vivo repair of a protein underlying a neurological disorder by programmable RNA editing
John R. Sinnamon, Susan Y. Kim, Jenna R. Fisk…·Gail Mandel
This study uses RNA base editing to repair a mutation in a mouse model of Rett syndrome, restoring MeCP2 function in hippocampal neurons.
67 citationstop 5%