PhysiologyMolecular TherapyPeer-reviewed
Neonatal systemic gene therapy restores cardiorespiratory function in a rat model of Pompe disease
David Dwight Fuller, Sabhya Denise Rana, Prajwal Pradeep Thakre…·Barry J. Byrne
4 citations
Author
University of Florida
Listed by name: these papers carry no ORCID for this author, so different people with the same name may be mixed together.
2 papers
Recent·Most cited
David Dwight Fuller, Sabhya Denise Rana, Prajwal Pradeep Thakre…·Barry J. Byrne
Armin Raznahan, Neelroop Parikshak, V. Ravi Chandran…·Daniel H. Geschwind
The paper investigates how sex chromosome dosage affects gene expression in humans by analyzing diverse aneuploidies and identifies SCD-sensitive genes and their regulatory networks.