Comparative Study of BBB-Targeting AAV Capsids on CentralNervous System Delivery Efficiency
Junhao Zhao, Xiangyu Ge, Minghui Song, Weimin Liu, Xia Zhang, Li Zuo, Lei Jin
This study compares BBB-targeting AAV capsids for CNS delivery efficiency and safety, finding CNSRCV300 offers the best balance between brain targeting and biosafety.
bioRxiv · Jan 21, 2026 · PreprintNeuroscience