GeneticsNature GeneticsPeer-reviewed
CRISPR-Cas9 Screens In Human Cells And Primary Neurons Identify Modifiers Of C9orf72 Dipeptide Repeat Protein Toxicity
Nicholas J. Kramer, Michael Seamus Haney, David W. Morgens…·Aaron D. Gitler
Genome-wide CRISPR-Cas9 screens in human cells reveal mechanisms and targets for ALS-associated C9orf72 dipeptide repeat protein toxicity.