NeuroscienceMolecular Therapy — Methods & Clinical DevelopmentPeer-reviewed
Optimizing AAV2/6 microglial targeting identified enhanced efficiency in the photoreceptor degenerative environment
Margaret E. Maes, Gabriele M Wögenstein, Gloria Colombo…·Sandra Siegert
The paper optimizes AAV2/6 for microglial targeting in the retina, showing enhanced transduction during photoreceptor degeneration through capsid modification and Cre-dependent cassette validation.
12 citations