Cell BiologybioRxivPreprint
Inhibition of acid ceramidase as a therapeutic strategy for Niemann-Pick C disease
Isabelle Haynes, Simon E. Ward, Dyfyr Heulyn Jones…·Helen Waller‐Evans
This study identifies acid ceramidase as a potential therapeutic target for Niemann-Pick C disease by reducing lipid accumulation in a cellular model.
DOI 10.1101/2024.11.13.623427