GeneticsbioRxivPreprint
Allele-specific antisense oligonucleotide treatment rescues atad3-associated phenotype in zebrafish
Shlomit Ezer, Shira Yanovsky‐Dagan, Amit Granit…·Tamar Harel
This study demonstrates that allele-specific antisense oligonucleotides can rescue ATAD3A-associated developmental defects in zebrafish by reducing mutant transcripts.
DOI 10.64898/2026.05.20.726050