Synthetic BiologybioRxivPreprint
Tunable Expression of an AAV Payload Using ADAR-mediated RNA Editing
Joseph Silverberg, Laura Pereira, Robert Schmidt…·Federico Mingozzi
This paper demonstrates an ADAR-mediated gene switch to control AAV-delivered gene expression by rescuing a premature termination codon via RNA editing, achieving tunable and clinically relevant therapeutic protein levels.
DOI 10.64898/2026.08.04.742838