BioengineeringMolecular Therapy — Methods & Clinical DevelopmentPeer-reviewed
Retinal organoids mirror CRISPR/Cas9 gene editing efficiency observed in vivo
Juliette Pulman, Hugo Malki, Paul Oudin…·Deniz Dalkara
The paper compares CRISPR/Cas9 gene editing efficiency in retinal organoids, HEK293T cells, and mouse models, finding retinal organoids better mirror in vivo editing outcomes.