GeneticsNature CommunicationsPeer-reviewed
PKD1 and PKD2 mRNA cis-inhibition drives polycystic kidney disease progression
Ronak Lakhia, Harini Ramalingam, Chun-Mien Chang…·Vishal Patel
This study identifies cis-inhibition of PKD1 and PKD2 mRNAs via miR-17 in ADPKD and shows that disrupting this mechanism reduces cyst growth in multiple models.