Cell BiologyScientific ReportsPeer-reviewed
TRPML1 activation ameliorates lysosomal phenotypes in CLN3 deficient retinal pigment epithelial cells
D. Wuenkhaus, R. Tang, K. Nyame…·S. Markmann
This study shows TRPML1 activation reduces lysosomal storage in CLN3-deficient retinal cells but does not restore BMP levels.
DOI 10.1038/s41598-024-67479-8