Cancer BiologybioRxiv
Indisulam targets RNA splicing and metabolism to serve as a novel therapeutic strategy for high-risk neuroblastoma
A. Nijhuis, A. Sikka, O. Yogev…·H. C. Keun
This study shows that indisulam, a sulphonamide, targets RNA splicing and metabolism to inhibit neuroblastoma growth and achieve complete tumor remission in preclinical models.